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기록
USE OF ARIMOCLOMOL IN ACTIVATING CLEAR GENE EXPRESSION AS TREATMENT FOR LYSOSOMAL STORAGE DISORDERS
발명심사 중
29청구항 · 8 독립항
§ Ⅰ
개요
발명자
Sven Guenther; Travis Mickle; Thomas Kirkegaard Jensen
IPC 분류
A61K 31/4545A61P 3/
CPC 분류
A61K31/4545A61P3/
The present disclosure provides methods of treating lysosomal storage disorders such as Niemann-Pick Disease, Type-C, by administering a therapeutically effective amount of arimoclomol. The present disclosure further provides methods of removing lysosomal cholesterol by administering the same.
원문 (중국어)
The present disclosure provides methods of treating lysosomal storage disorders such as Niemann-Pick Disease, Type-C, by administering a therapeutically effective amount of arimoclomol. The present disclosure further provides methods of removing lysosomal cholesterol by administering the same.